完成研究
学习MPSVI CSP
粘多糖病(MPS) VI临床监测项目(CSP)
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指示
粘多糖病VI (议员六世, Maroteaux-Lamy综合征)
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临床实验的治疗
Naglazyme® (galsulfase)
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研究类型
第四阶段
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Goal
The objectives of this program are: to further characterize the natural progression of 议员六世 disease; to generate and disseminate information on the care and management of 议员六世 patients to clinical and medical professionals; to provide a resource to physicians and patients by providing information for optimizing patient care based on aggregate data; to characterize the clinical response to long-term Naglazyme® (galsulfase) 治疗; to further characterize the long-term safety of Naglazyme® 治疗.
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状态
本研究已经完成