澳门十大博彩正规游戏平台 Approves 澳门正规博彩十大排行平台’s Gene Therapy for a Genetic Bleeding Disorder
We’re thrilled to share that the U.S. Food and Drug Administration has approved our gene therapy for a genetic bleeding disorder. Developing the one-time therapy and bringing it over the finish line, first in Europe and now the United States, has been a global effort. Our teams have made unprecedented scientific, medical, manufacturing and regulatory […]
A Message from the Chairman and CEO
Dear Stockholder of 澳门正规博彩十大排行平台: In 2022, 澳门正规博彩十大排行平台 achieved record revenue and pivoted to GAAP profitability, making it a truly transformational year for the company and laying the foundation for long-term growth. The global launch of VOXZOGO for children with achondroplasia helped drive that revenue growth. We believe conditional European approval of our gene therapy for […]
Enduring Purpose, Expanding Reach
As we reflect on the progress of the last quarter century, we take this opportunity to also look forward to what’s next for 澳门正规博彩十大排行平台. In our continued pursuit to maximize impact for patients, we continue to ask ourselves: what more can we do? The outcome of this ongoing self-assessment has helped bring clarity to how we can best deliver on our purpose – to transform lives through genetic discovery.